by Dr. Yashashwini Reddy | Sep 24, 2025
Case Study: Zolgensma (Novartis) – The World’s Most Expensive Drug Background Drug: Zolgensma (onasemnogene abeparvovec) Company: Novartis Gene Therapies (AveXis subsidiary) Indication: Spinal Muscular Atrophy (SMA) – a rare, often fatal genetic disorder in infants....
by Dr. Yashashwini Reddy | Jun 2, 2024
How orphan drug designation is given in Japan In the previous articles we have studied orphan drugs and now we are going to learn about how orphan drug designation is given in Japan, we are going to discuss how and what are the laws guiding orphan drug designation in...
